Applications of Lentiviral Vectors for Biology and Gene Therapy of Neurological Disorders
Gene therapy clinical trials in the human brain. Protocol development and review of current applications
Prospects for gene therapy in inherited neurodegenerative diseases (2007)
Therapeutic strategies against protein misfolding in neurodegenerative diseases
Intravenous, non-viral RNAi gene therapy of brain cancer (2006)
Targeting of retroviral vectors for gene therapy (1993)

AAV natural infection induces broad cross-neutralizing antibody responses to multiple AAV serotypes in chimpanzees
Gene Editing for Treatment of Neurological Infections
Engineering of a Stable Retroviral Gene Delivery Vector by Directed Evolution
Directed evolution of adeno-associated virus for enhanced gene delivery and gene targeting in human pluripotent stem cells
Engineered AAVs for efficient noninvasive gene delivery to the central and peripheral nervous systems
Inhibition of antigen presentation during AAV gene therapy using virus peptides
Extracellular vesicles: nature's nanoparticles for improving gene transfer with adeno-associated virus vectors
Mycophenolate mofetil impairs transduction of single-stranded adeno-associated viral vectors
Modulation of tolerance to the transgene product in a nonhuman primate model of AAV-mediated gene transfer to liver
Proteasome inhibitors decrease AAV2 capsid derived peptide epitope presentation on MHC class I following transduction
Capsid antigen presentation flags human hepatocytes for destruction after transduction by adeno-associated viral vectors
Engineered AAV vector minimizes in vivo targeting of transduced hepatocytes by capsid-specific CD8+ T cells
Humoral immunity to AAV vectors in gene therapy: challenges and potential solutions
Development of patient-specific AAV vectors after neutralizing antibody selection for enhanced muscle gene transfer
Structure-guided evolution of antigenically distinct adeno-associated virus variants for immune evasion
Immunological monitoring to rationally guide AAV gene therapy
Gene therapy research at the Frontiers of viral immunology
Engineering delivery vehicles for genome editing
Beyond humanization and de-immunization: tolerization as a method for reducing the immunogenicity of biologics
Superior in vivo transduction of human hepatocytes using engineered AAV3 capsid
Surface-engineered viral vectors for selective and cell type-specific gene delivery
Humoral immunity to AAV vectors in gene therapy: challenges and potential solutions
Use of genetically modified mesenchymal stem cells to treat neurodegenerative diseases